Spinal muscular atrophy

'I knew Snowdon would be a challenge'

'Ticking time bomb' for service after staff change

'Atlantic' challenge to fund toddler's treatment

Indians who need a $2.1m drug to fight rare disease

Twins forecast not to live past seven turn 18

'Without an assistant I can only shower once a week'

India teen who died but raised millions to save brother

Baby blood test 'could prove life-changing'

Trial to screen pregnant women for muscle condition

Baby given £1.79m drug takes first assisted steps. Video, 00:01:27Baby given £1.79m drug takes first assisted steps

Baby given £1.79m drug has new lease of life

The TikTok star busting disability myths online. Video, 00:02:28The TikTok star busting disability myths online

Double act teen twins search for support. Video, 00:02:26Double act teen twins search for support

Lockdown and the cost of cancelled physio sessions

'Miracle drug' treatment for boy's rare disorder

Baby given £1.79m drug makes 'huge progress'

Parents 'so excited' after baby given £1.79m drug

Parents 'ecstatic' after baby granted £1.7m drug

Baby 'doing OK' after spinal gene therapy first

Baby one of first to get new spinal gene therapy

'Gene therapy is a game changer for our son'

Dad hopes baby could be saved by 'game changer' drug. Video, 00:00:47Dad hopes baby could be saved by 'game changer' drug

Parents hoping for £1.7m drug 'feel abandoned'